Activities Report / Information listREPORT & INFORMATION
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2025.02.03
Medical and disease
informationBasic Knowledge of Lysosomal Storage Diseases-Overview NEW
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2025.01.06
Medical and disease
informationResearch and Development of Lysosomal Storage Diseases
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2024.12.02
Useful information
Patient Advocacy Groups: A Place for Mutual Support and Information Sharing
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2024.11.01
Medical and disease
informationCurrent Status and Future Prospects of Decentralized Clinical Trials (DCTs)
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2024.10.01
Medical and disease
informationWhat is the relationship between Real-World Data and Healthcare?
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2024.06.03
Useful information
The Journey of New Drug Development
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2024.05.07
Activity report
“Rare Disease Week 2024” disease awareness event held for employees at Tokyo Head Office
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2024.04.01
Medical and disease
informationDisease Information “Mucopolysaccharidosis type III (Sanfilippo syndrome)”
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2024.04.01
Useful information
Introduction to Clinical Trial Database
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2024.02.29
Activity report
20th Annual WORLDSymposiumTM 2024 Report
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2024.02.29
Activity report
The 28th Annual Meeting of the Japanese Society for Lysosomal Storage Diseases Report
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2024.02.29
Activity report
The 64th Annual Meeting of the Japanese Society for Inherited Metabolic Diseases Report
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2024.01.22
Medical and disease
informationTerms
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2024.01.22
Activity report
19th Annual WORLDSymposiumTM 2023 Report
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2024.01.22
Medical and disease
informationDisease information “Fucosidosis”
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2023.09.28
News releases
Initiatives to realize delivery of medicines for rare diseases to individual homes: Private residence delivery enables continued treatment for patients who have difficulty going to the hospital (For Japan)【PDF】
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2023.01.26
News releases
Announcement of starting a trial for delivery to the homes of patients who have difficulty going to the hospital (For Japan)【PDF】
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2023.01.18
News releases
Initiatives to realize delivery of medicines for rare diseases to individual homes (For Japan)【PDF】