Rare disease Insights for EveryOne

Activities Report / Information

What we want to deliver

REPORT & INFORMATIONActivities Report / Information

We provide a wide range of useful information on rare diseases, especially in the area of lysosomal storage diseases.

Research and Development of Lysosomal Storage Diseases ^NEW
2024.07.01
- #Lysosomal storage diseases
- #Clinical trial for regulatory submission
- #Clinical trial
The Journey of New Drug Development
2024.06.03
- #New drugs development
- #Clinical trial for regulatory submission
- #Clinical trial
“Rare Disease Week 2024” disease awareness event held for employees at Tokyo Head Office
2024.05.07
- #Rare disease
- #Rare disease day
- #Disease awareness
Introduction to Clinical Trial Database
2024.04.01
- #Clinical trial for regulatory submission
- #Clinical trial
20th Annual WORLDSymposium^TM 2024 Report
2024.02.29
- #Lysosomal storage disease
- #Participation report
- #Patient association
- #Mucopolysaccharidosis type III
The 28th Annual Meeting of the Japanese Society for Lysosomal Storage Diseases Report
2024.02.29
- #Lysosomal storage disease
- #Participation report

Article list

PICK UPTopics on rare diseases

We have selected information about rare diseases that we desire for everyone to know.

Disease Information ‘Mucopolysaccharidosis type III (Sanfilippo syndrome)’
2024.04.01
- #Lysosomal storage diseases
- #Mucopolysaccharidosis type III
- #Sanfilippo syndrome
Disease information 'Fucosidosis'
2024.01.22
- #Lysosomal storage diseases
- #Fucosidosis

WHAT WE WANT TO DELIVEROur target initiatives

Provide new medications throughout the world

It is our desire to provide new medications to patients around the world.

Deliver medications and information

We desire to provide medications and information to each and every person who needs it.

ABOUTOur desires

Make your smile, Brighten your future

We put up “Expand, Support, and Connect ‘Pharmaceuticals, Health, and Beauty’” as the “ideal situation”, and we are developing various business activities to contribute to the healthy lives of people. For rare diseases, we have been making use of our Group’s strong distribution capabilities by providing development support to pharmaceutical companies ("PFM^Ⓡ") and establishing ultra-low temperature control logistics technology. Since 2022, as a new initiative, we have been taking on the challenge of developing pharmaceuticals in cooperation with JCR Pharmaceuticals Co., Ltd. and delivering to patients globally in the field of ultra-rare diseases, where the number of patients is particularly small.

The theme of this website is “Make your smile, Brighten your future,” and we will provide useful information to bring smiles to as many patients with rare diseases and their families as possible. By exchanging and disclosing information with patients, their families, and healthcare professionals, we hope to develop this site as a place where patients, medical treatment, pharmaceuticals, and distribution can unite and connect.

PFM^Ⓡ：Project Finance & Marketing
A business model where risks and returns are shared with pharmaceutical companies through investment in medication development

Image of medical care that empathizes with patients

The disease is known to exist, and the doctors exist.
But there is no treating medication.
What can we do to address the realities of rare diseases?
We believe that this means being close to the desires of the patients and their families, and developing and reliably delivering innovative pharmaceuticals that are not yet available in the world. The MEDIPAL Group will continue to take on the challenge not only in Japan but also on a global scale of nurturing invaluable life by envisioning the healthy upbringing of the world's children who will carry our future.